Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)

NCT06948019 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

NOT_YET_RECRUITING

Status

5

Enrollment

INDUSTRY

Sponsor class

Conditions

HSP
Hereditary Spastic Paraplegia
Hereditary Spastic Paraparesis
Hereditary Spastic Paraplegia Type 50
Hereditary Spastic Paraplegia Type 47
Hereditary Spastic Paraplegia Type 51
Hereditary Spastic Paraplegia Type 52
SPG47
AP4B1
Neurogenetic Disorders
Neurodevelopmental Conditions
Movement Disorders
Gene Therapy

Interventions

BIOLOGICAL: BFB-101 (AAV9-CBh-AP4B1)

Sponsor

BlackfinBio Ltd

Collaborators

[object Object]