# Gene Therapy for Alpha 1- Antitrypsin Deficiency

> **NCT06996756** · PHASE1 · RECRUITING · sponsor: **Weill Medical College of Cornell University** · enrollment: 16 (estimated)

## Conditions studied

- Alpha 1-Antitrypsin Deficiency

## Interventions

- **BIOLOGICAL:** AAV8hAAT(AVL)

## Key facts

- **NCT ID:** NCT06996756
- **Lead sponsor:** Weill Medical College of Cornell University
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2025-02-26
- **Primary completion:** 2028-04-30
- **Final completion:** 2032-08-01
- **Target enrollment:** 16 (ESTIMATED)
- **Last updated:** 2026-03-13

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06996756

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06996756, "Gene Therapy for Alpha 1- Antitrypsin Deficiency". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT06996756. Licensed CC0.

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