RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)

NCT07014020 · clinicaltrials.gov ↗

NA

Phase

RECRUITING

Status

8

Enrollment

OTHER

Sponsor class

Conditions

Phelan-McDermid Syndrome
SHANK3 Haploinsufficiency

Interventions

GENETIC: RB001

Sponsor

Peking University First Hospital

Collaborators

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