Ivacaftor Impact in an Adolescent Without a Cystic Fibrosis-Associated CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) Mutation for Chronic Pancreatitis: Single-Patient Study Tracking Flare Frequency and Health Data Compared to Historical Records.
ACTIVE_NOT_RECRUITING
Status
Conditions
Interventions
- DRUG: Ivacaftor 150 MG (milligrams)
Sponsor
Mission: Cure