# Efficacy and Safety of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

> **NCT07054632** · PHASE3 · ACTIVE_NOT_RECRUITING · sponsor: **Innostellar Biotherapeutics Co.,Ltd** · enrollment: 30 (actual)

## Conditions studied

- Inherited Retinal Dystrophy Associated With RPE65 Mutations

## Interventions

- **GENETIC:** LX101

## Key facts

- **NCT ID:** NCT07054632
- **Lead sponsor:** Innostellar Biotherapeutics Co.,Ltd
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2023-09-13
- **Primary completion:** 2025-08-13
- **Final completion:** 2029-08
- **Target enrollment:** 30 (ACTUAL)
- **Last updated:** 2026-03-05


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07054632

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07054632, "Efficacy and Safety of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations". Retrieved via AI Analytics 2026-06-04 from https://api.ai-analytics.org/clinical/NCT07054632. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*