Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1

NCT07070999 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

RECRUITING

Status

22

Enrollment

INDUSTRY

Sponsor class

Conditions

Spinal Muscular Atrophy Type I

Interventions

BIOLOGICAL: GB221

Sponsor

Gemma Biotherapeutics