# Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.

> **NCT07080268** · — · ACTIVE_NOT_RECRUITING · sponsor: **Hospital General de Niños Pedro de Elizalde** · enrollment: 70 (estimated)

## Conditions studied

- Amyloidosis in Transthyretin (TTR)
- Hereditary Amyloidosis, Transthyretin-Related

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT07080268
- **Lead sponsor:** Hospital General de Niños Pedro de Elizalde
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2025-06-20
- **Primary completion:** 2025-09-01
- **Final completion:** 2025-12-30
- **Target enrollment:** 70 (ESTIMATED)
- **Last updated:** 2025-07-23


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07080268

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07080268, "Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT07080268. Licensed CC0.

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