# Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation

> **NCT07125898** · — · NOT_YET_RECRUITING · sponsor: **Assistance Publique - Hôpitaux de Paris** · enrollment: 110 (estimated)

## Conditions studied

- Dystrophinopathies

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT07125898
- **Lead sponsor:** Assistance Publique - Hôpitaux de Paris
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** NOT_YET_RECRUITING
- **Start date:** 2025-10-01
- **Primary completion:** 2027-10-01
- **Final completion:** 2029-04-01
- **Target enrollment:** 110 (ESTIMATED)
- **Last updated:** 2025-08-15


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07125898

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07125898, "Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT07125898. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
