Gene Therapy for SLC6A1 Neurodevelopmental Disorder
NCT07173153
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
ENROLLING_BY_INVITATION
Status
1
Enrollment
OTHER
Sponsor class
Conditions
SLC6A1
Interventions
BIOLOGICAL:
AAV9.SLC6A1 Gene Therapy
Sponsor
Emily de los Reyes