Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) Patients
NCT07188012
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
RECRUITING
Status
9
Enrollment
INDUSTRY
Sponsor class
Conditions
Duchenne Muscular Dystrophy (DMD)
Interventions
GENETIC:
SPOT-03
Sponsor
Shanghai Siponuoyin Biotechnology Co Ltd
Collaborators
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