# Confirmatory Study of Govorestat in CMT-SORD

> **NCT07191912** · PHASE3 · NOT_YET_RECRUITING · sponsor: **Applied Therapeutics, Inc.** · enrollment: 155 (estimated)

## Conditions studied

- Charcot-Marie-Tooth Disease With Sorbitol Dehydrogenase Deficiency (CMT-SORD)

## Interventions

- **DRUG:** Govorestat
- **DRUG:** Placebo Control

## Key facts

- **NCT ID:** NCT07191912
- **Lead sponsor:** Applied Therapeutics, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** NOT_YET_RECRUITING
- **Start date:** 2025-10
- **Primary completion:** 2028-10
- **Final completion:** 2029-01
- **Target enrollment:** 155 (ESTIMATED)
- **Last updated:** 2025-09-25


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07191912

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07191912, "Confirmatory Study of Govorestat in CMT-SORD". Retrieved via AI Analytics 2026-06-24 from https://api.ai-analytics.org/clinical/NCT07191912. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
