Natural History Study for Patients With Nemaline Myopathy in Belgium

NCT07201636 · clinicaltrials.gov ↗

NA

Phase

NOT_YET_RECRUITING

Status

10

Enrollment

OTHER

Sponsor class

Conditions

Nemaline Myopathy

Interventions

DIAGNOSTIC_TEST: Motor Function Assessments
DEVICE: Syde
DIAGNOSTIC_TEST: Respiratory Assessments
DIAGNOSTIC_TEST: Bulbar Function Questionnaires
DIAGNOSTIC_TEST: Clinical Global Impression (CGI)
OTHER: Quality of Life Questionnaires
PROCEDURE: Blood Sample Collection

Sponsor

Centre Hospitalier Universitaire de Liege

Collaborators

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