# Natural History Study for Patients With Nemaline Myopathy in Belgium

> **NCT07201636** · NA · NOT_YET_RECRUITING · sponsor: **Centre Hospitalier Universitaire de Liege** · enrollment: 10 (estimated)

## Conditions studied

- Nemaline Myopathy

## Interventions

- **DIAGNOSTIC_TEST:** Motor Function Assessments
- **DEVICE:** Syde
- **DIAGNOSTIC_TEST:** Respiratory Assessments
- **DIAGNOSTIC_TEST:** Bulbar Function Questionnaires
- **DIAGNOSTIC_TEST:** Clinical Global Impression (CGI)
- **OTHER:** Quality of Life Questionnaires
- **PROCEDURE:** Blood Sample Collection

## Key facts

- **NCT ID:** NCT07201636
- **Lead sponsor:** Centre Hospitalier Universitaire de Liege
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** NOT_YET_RECRUITING
- **Start date:** 2026-08
- **Primary completion:** 2029-04
- **Final completion:** 2029-08
- **Target enrollment:** 10 (ESTIMATED)
- **Last updated:** 2026-03-25

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07201636

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07201636, "Natural History Study for Patients With Nemaline Myopathy in Belgium". Retrieved via AI Analytics 2026-05-24 from https://api.ai-analytics.org/clinical/NCT07201636. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
