Double-Blind Trial of Everolimus for Improving Social Abilities in PTEN Germline Mutations
Conditions
- Cowden's Disease
- Cowden's Syndrome
- Lhermitte-Duclos Disease
- Cerebellum Dysplastic Gangliocytoma
- Bannayan Zonana Syndrome
- Myhre Riley Smith Syndrome
- Riley Smith Syndrome
- PTEN Hamartoma Tumor Syndrome
- Bannayan Riley Ruvalcaba Syndrome
Interventions
- DRUG: Everolimus blinded oral capsules
- DRUG: Placebo
Sponsor
Boston Children's Hospital