Treatment of Charcot-Marie-Tooth Disease, Axonal, Type 2S (CMT2S) in an Individual Patient
NCT07223632
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
ACTIVE_NOT_RECRUITING
Status
1
Enrollment
INDUSTRY
Sponsor class
Conditions
Charcot Marie Tooth Disease (CMT)
Neuromuscular Diseases (NMD)
Interventions
DRUG:
VCA-894A
Sponsor
Vanda Pharmaceuticals