Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV
NCT07398872
·
clinicaltrials.gov ↗
PHASE1
Phase
ENROLLING_BY_INVITATION
Status
1
Enrollment
OTHER
Sponsor class
Conditions
Mucolipidosis Type IV
Interventions
BIOLOGICAL:
AAV9.hMCOLN1co
Sponsor
The Children's Hospital of Zhejiang University School of Medicine