# Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV

> **NCT07398872** · PHASE1 · ENROLLING_BY_INVITATION · sponsor: **The Children's Hospital of Zhejiang University School of Medicine** · enrollment: 1 (estimated)

## Conditions studied

- Mucolipidosis Type IV

## Interventions

- **BIOLOGICAL:** AAV9.hMCOLN1co

## Key facts

- **NCT ID:** NCT07398872
- **Lead sponsor:** The Children's Hospital of Zhejiang University School of Medicine
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** ENROLLING_BY_INVITATION
- **Start date:** 2026-01-13
- **Primary completion:** 2027-01-20
- **Final completion:** 2031-01-20
- **Target enrollment:** 1 (ESTIMATED)
- **Last updated:** 2026-02-10


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07398872

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07398872, "Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT07398872. Licensed CC0.

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