Assess Long-Term Safety of Danicopan Add-on Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria: Analysis of IPIG-Registry Data
ACTIVE_NOT_RECRUITING
Status
Conditions
- Paroxysmal Nocturnal Hemoglobinuria
- PNH
Interventions
- DRUG: Danicopan
- DRUG: Soliris/Ultomiris
Sponsor
Alexion Pharmaceuticals, Inc.