PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
Conditions
- Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD
Interventions
- BIOLOGICAL: PBGENE-DMD (IV)
Sponsor
Precision BioSciences, Inc.