# A Single Patient Study of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome

> **NCT07574034** · NA · NOT_YET_RECRUITING · sponsor: **Gregor Andelfinger** · enrollment: 1 (estimated)

## Conditions studied

- Multisystemic Smooth Muscle Dysfunction Syndrome

## Interventions

- **DRUG:** Kuvan (Sapropterine)

## Key facts

- **NCT ID:** NCT07574034
- **Lead sponsor:** Gregor Andelfinger
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** NOT_YET_RECRUITING
- **Start date:** 2026-06-01
- **Primary completion:** 2028-06-01
- **Final completion:** 2030-06-01
- **Target enrollment:** 1 (ESTIMATED)
- **Last updated:** 2026-05-07


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07574034

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07574034, "A Single Patient Study of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome". Retrieved via AI Analytics 2026-08-09 from https://api.ai-analytics.org/clinical/NCT07574034. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*