Development of a new drug for treating autoimmune uveitis

NIH RePORTER · NIH · R41 · $255,388 · view on reporter.nih.gov ↗

Abstract

Summary Autoimmune uveitis is a major cause of blindness in which retinal antigen-specific T cells lead to ocular inflammation and vision loss. Similar to the treatment of other T cell-mediated autoimmune diseases, selective suppression of the pathogenic T cells is the “holy grail” of therapeutic development. In pilot studies, we have developed a novel antibody-drug conjugate (ADC) with combined T cell targeting and potent anti-mitosis activity, which is designed to selectively kill the proliferating autoreactive T cells while sparing the other cells including normal T cells. In this Phase I application, we will first demonstrate that this ADC selectively kills proliferating uveitogenic T cells while sparing normal T cells and other cells both in vitro and in vivo, then determine its in vivo treatment efficacy and potential off-target effects in two animal models of autoimmune uveitis. These studies will provide the required proof-of-concept for a Phase II development of this promising ADC towards IND-enabling studies and further clinical development.

Key facts

NIH application ID
10321980
Project number
1R41EY033243-01
Recipient
ABCON THERAPEUTICS, INC.
Principal Investigator
FENG C LIN
Activity code
R41
Funding institute
NIH
Fiscal year
2021
Award amount
$255,388
Award type
1
Project period
2021-09-01 → 2023-08-31