Metabolically improving the generation, function, and persistence of therapeutic T cells for the treatment of cancer

NIH RePORTER · NIH · F31 · $46,752 · view on reporter.nih.gov ↗

Abstract

Project Summary Immunotherapy has shifted the paradigm in the understanding and treatment of cancer. Within this arsenal of new treatment strategies, adoptive cell therapy (ACT) has shown great promise; however, several barriers to efficacy remain. One major hurdle is the high metabolic requirements of T cell anti-tumor cytoxicity within the nutrient-poor tumor microenvironment (TME). Current culturing strategies used to generate high numbers of T cells in vitro exacerbate this problem by using hyperglycemic and hyperoxic culture conditions. This strategy favors the metabolic needs of T cells during expansion but ignores their metabolic requirements for persistence within the TME. Our preliminary data indicate that treatment with the pyruvate dehydrogenase kinase 1 (PDHK1) inhibitor dichloroacetate (DCA) during in vitro expansion of therapeutic T cells maintains therapeutic T cell proliferation while improving anti-tumor clearance in vivo. Intriguingly, transcriptomic analysis of DCA-treated T cells reveals a downregulation of interferon-stimulated genes (ISGs) seen in response to mitochondrial DNA (mtDNA) damage. We hypothesize that DCA shunts glycolysis in a manner that re-directs metabolism to a more oxidative state and thus prevents T cell mitochondrial stress and mtDNA releases during initial expansion allowing for more fit T cells pre-infusion. Within this study, we aim to determine how DCA’s metabolic effects and abrogation of ISGs contribute to improved anti-tumor efficacy. Determining the mechanism of action of DCA on therapeutic T cells will not only inform the field of the benefits of using DCA as an in vitro culture supplement for the generation of more efficacious therapeutic T cells, but will also allow for a better understanding of the biological requirements for T cell function overall.

Key facts

NIH application ID
10348167
Project number
5F31CA257760-02
Recipient
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
Principal Investigator
Andrew Frisch
Activity code
F31
Funding institute
NIH
Fiscal year
2022
Award amount
$46,752
Award type
5
Project period
2021-02-01 → 2023-01-31