Aptamer-based LYTACs to screen for critical determinants of lysosomal degradation

NIH RePORTER · NIH · R01 · $1,388 · view on reporter.nih.gov ↗

Abstract

PROJECT ABSTRACT Extracellular and transmembrane proteins are central pathological components in cancer, aging-related disorders, and autoimmune disease. These proteins can be degraded using lysosome targeting chimeras (LYTACs), antibodies conjugated to polymeric chemical moieties engaging the cation-independent mannose-6- phosphate receptor (CI-M6PR). As these molecules require careful chemical synthesis, we will produce alternate LYTACs in high throughput using aptamers targeting CI-M6PR linked to nanobodies via enzymatic autoconjugation. This method will help elucidate optimal LYTAC binding affinities to CI-M6PR. We will further use enzymatic autoconjugation to produce aptamer-LYTACs within bacterial cells in a genetically-encoded fashion, enabling future work to define the LYTACable proteome.

Key facts

NIH application ID
10393856
Project number
3R01GM058867-23S1
Recipient
STANFORD UNIVERSITY
Principal Investigator
Carolyn Bertozzi
Activity code
R01
Funding institute
NIH
Fiscal year
2021
Award amount
$1,388
Award type
3
Project period
1999-01-01 → 2024-06-30