New classes of optogenetic and chemogenetic tools with a feedback control

NIH RePORTER · NIH · DP2 · $1,350,000 · view on reporter.nih.gov ↗

Abstract

New classes of optogenetic and chemogenetic tools with a feedback control Project Summary Optogenetic and chemogenetic tools have revolutionized neuroscience research. They also hold great promise for gene therapy of neurological disorders, such as epilepsy, schizophrenia and anxiety disorders. For example, among the ~ 65 million people worldwide affected by epilepsy, 30% of them are resistant to current medicine but could significantly benefit from new therapies that can quickly and effectively suppress the irregular neuronal activities during seizures. However, we currently lack tools for prolonged neuronal silencing with fast response to precisely modulate the irregular neuronal activities in neurological disorders for both neuroscience research and therapeutic development. The state-of-the-art optogenetic tools for neuromodulation provide fast temporal control via light, but they are limited by light-induced tissue heating in long-lasting neuronal silencing experiments. Existing chemogenetic tools are effective for long-term neuronal silencing, however, they are limited by their slow on/off rate due to drug administration. There is a need of new tools that will enable prolonged neuronal silencing in quick response to the irregular neuronal activities in neurological disorders. Our long-term goal is to engineer modular biological designs for controlling the activities of specific neuronal pathways with tunable temporal control and minimal invasiveness for neuroscience research and potential therapeutics. In this application, we propose to design the first closed- loop chemogenetic tool with a feedback control to suppress the irregularly-high neuronal activities, and a highly-light-sensitive optogenetic tool to achieve long-lasting silencing of neuronal activities. These new tools based on membrane-tethered temporally-gated peptide agonists for G-protein-coupled receptors are highly innovative and modular, and will open up a new frontier in designing neuromodulation tools for manipulating neuronal pathways. They will also advance the basic research on neuronal circuitry and facilitate the development of potential therapeutics for manipulating neuronal pathways in patients with neurological disorders.

Key facts

NIH application ID
10469777
Project number
1DP2MH132939-01
Recipient
UNIVERSITY OF MICHIGAN AT ANN ARBOR
Principal Investigator
Wenjing Wang
Activity code
DP2
Funding institute
NIH
Fiscal year
2022
Award amount
$1,350,000
Award type
1
Project period
2022-08-15 → 2025-08-14