S4 TO 108 NCATS GENE THERAPY VECTOR

NIH RePORTER · NIH · N02 · $3,795,000 · view on reporter.nih.gov ↗

Abstract

Produce and deliver a research grade gene therapy vector for a potential lead candidate for hereditary methylmalonic acidemias using AAV9 platform-based gene therapy vector platform.

Key facts

NIH application ID: 10497626
Project number: 75N98020D00086-0-759802100357-1
Recipient: MEDICAL SCIENCE & COMPUTING, LLC
Principal Investigator: ANNA KOROLEVA
Activity code: N02
Funding institute: NIH
Fiscal year: 2021
Award amount: $3,795,000
Award type: —
Project period: 2021-09-30 → 2022-12-31