HTS to identify compounds that increase NAD+ levels in neurons and muscle cells

NIH RePORTER · NIH · R33 · $279,416 · view on reporter.nih.gov ↗

Abstract

Project Summary Nicotinamide adenine dinucleotide (NAD) is a redox cofactor required by enzymes essential to energy production and numerous other cellular processes. NAD also serves as a co-substrate for several classes of signaling enzymes, each of which cleaves the molecule to release nicotinamide. Cellular NAD is derived from dietary tryptophan (de novo synthesis), nicotinic acid (the Preiss-Handler pathway) or recycled from nicotinamide via the NAD salvage pathway. NAD deficiency can be triggered by a variety of cellular stresses, including DNA damage, and is thought to contribute to pathophysiology in a number of metabolic, neurological, and muscular diseases: conversely, increasing NAD+ has been suggested as a promising therapeutic strategy. Here, researchers will collaborate to develop and utilize a cellular High Throughput Screening (HTS) assay to discover and validate small molecules that increase intracellular NAD+ levels. These studies should identify novel small molecules with great therapeutic potential for a myriad of neurological and muscular including brain ischemia, Wallerian nerve degeneration, misfolded prion protein toxicity, Alzheimer's disease (AD), mitochondrial myopathy (MM), age related sarcopenia and Duchenne's muscular dystrophy(DMD).

Key facts

NIH application ID
10618481
Project number
4R33NS111375-02
Recipient
UNIVERSITY OF PENNSYLVANIA
Principal Investigator
Joseph A. Baur
Activity code
R33
Funding institute
NIH
Fiscal year
2022
Award amount
$279,416
Award type
4N
Project period
2022-06-01 → 2024-05-31