Stroma penetrating and immune modulating nanoparticles for image-guided therapy of pancreatic cancer

NIH RePORTER · NIH · R01 · $28,146 · view on reporter.nih.gov ↗

Abstract

Project Summary Recent advances in targeted delivery of nanoparticle/drugs and CAR T cell therapy have shown promises in the development of novel approaches for overcoming resistance to chemo- and immunotherapy in pancreatic cancer. A major obstacle in CAR T therapy in pancreatic cancer is the presence of multiple barriers that prevent cytotoxic T cells reaching tumors and actively killing tumor cells. Dense tumor stromal cells and extracellular matrix create physical and biological barriers to trap T cells in the stroma and inhibit T cell function. There is an unmet need of effective approaches to improve delivery of CAR T cells in pancreatic cancer. Tumor targeted, stroma- penetrating theranostic iron oxide nanoparticles (IONPs) developed in the parent R01 project offer an opportunity to develop a combination therapy to improve targeted delivery and intratumoral distribution of CAR T cells and overall therapeutic responses. Our results showed that uPAR-targeted and stroma breaking ligand (ATFmmp14) can overcome stromal cellular and extracellular matrix barriers to enhance tumor delivery of nanoparticle-drugs and T cells in human pancreatic PDX and transgenic mouse tumor models. In this supplement research project, we hypothesize that the binding of uPAR targeted, stroma-penetrating IONPs carrying chemo- and immunotherapeutic agents to CAR T cells significantly enhances delivery of CAR T cells and chemotherapy drugs into pancreatic cancer. Immune checkpoint PD-L1 and CTLA4 blocking peptides conjugated on the IONPs further activate CAR T cell function. Those combined effects lead to a strong therapeutic response in pancreatic cancer and overcome therapy resistance. In the proposed study, we will first determine the effect of ATFmmp14- conjugated IONPs carrying a chemotherapy agent, SN38, on viability and cytotoxicity of anti-MUC16 and/or Mesothelin CAR T cells in vitro in human pancreatic cancer cell lines. Therapeutic effect of co-delivery of the targeted IONP/SN38 with CAR T cells will be evaluated in a pancreatic cancer PDX model in SCID mice (Aim 1). Next, we will develop a novel targeted and stroma-penetrating CAR T cell delivery system by backpacking with ATFmmp14-IONP/SN38 carrying PD-L1 and/or CTLA4 blocking peptides, mediated by a CXCR4 inhibitor (BL-8040), for overcoming resistance to chemo- and CAR T cell therapy in pancreatic cancer (Aim 2). The effect on targeted delivery of CAR T cells and therapeutic efficacy using the backpack system containing ATFmmp14- IONP/SN38/immune checkpoint inhibitors will be evaluated in the pancreatic cancer PDX model (Aim 2). We will then investigate the therapeutic effects of the targeted chemo- and immunotherapy IONP-CAR T cells on tumor cells, immune cells and tumor stroma immune microenvironment using a mouse anti-MUC16 CAR T cells in a transgenic mouse pancreatic cancer cell line derived mouse tumor model (Aim 2). Finally, the feasibility of MR imaging for tracking intratumoral delivery of targeted...

Key facts

NIH application ID
10747717
Project number
3R01CA261251-02S1
Recipient
EMORY UNIVERSITY
Principal Investigator
Hui Mao
Activity code
R01
Funding institute
NIH
Fiscal year
2023
Award amount
$28,146
Award type
3
Project period
2023-03-01 → 2026-06-30