Genetic studies of a pleiotropic transmembrane protease: insight from color variation in non-model organisms

NIH RePORTER · NIH · R01 · $665,448 · view on reporter.nih.gov ↗

Abstract

Project Summary/Abstract Mendelian variation in pigmentation is a rich genetic resource to identify and study signaling pathways relevant to human biology, but the repertoire of mutations that affect pigmentation in mice and in humans coat color has become saturated. Advances in genome sequencing technology now extend the reach of forward genetics beyond humans and model organisms to domestic and wild animals, for which there are many pigmentary phenotypes likely to represent conserved signaling pathways but whose molecular basis is unknown. Using pigmentary variation in domestic cats, our research group discovered a striking connection between a novel transmembrane protease encoded by Transmembrane aminopeptidase Q (Taqpep) and a secreted Wnt inhibitor encoded by Dickkopf 4 (Dkk4). Initial studies of Taqpep knockout mice reveal a role in multiple cell types and tissues including hair, the enteric nervous system, and the palate. In a different non-model organism, the plains zebra, Taqpep is a candidate gene for aberrant striping in an isolated population in Rwanda. Our results point to a central role for Taqpep in pathways and tissues that are directly relevant to human biology and disease, but a molecular understanding of those pathways is most effectively approached by combining forward genetics for gene discovery in non-model mammalian organisms with experimental genetics in laboratory mice and studies in cultured mammalian cells. We propose to: (1) Identify additional components of Taqpep action by forward genetics in Bengal cats and by analysis of fetal cat skin (2) Expand initial genetic studies of color pattern variation in zebras (3) Determine the mechanism of Taqpep action using experimental mouse genetics and proteomics

Key facts

NIH application ID
10899629
Project number
5R01AR082708-03
Recipient
STANFORD UNIVERSITY
Principal Investigator
Gregory Stefan Barsh
Activity code
R01
Funding institute
NIH
Fiscal year
2024
Award amount
$665,448
Award type
5
Project period
2024-01-01 → 2028-06-30