DRUG DISCOVERY BY DIRECTED EVOLUTION IN MAMMALIAN CELLS

NIH RePORTER · NIH · K99 · $98,161 · view on reporter.nih.gov ↗

Abstract

Project Summary Directed evolution, which adopts principles of natural evolution to the laboratory, is singular in its impact on molecular engineering. As one example, it is responsible for the generation of the majority of approved therapeutic antibodies and those still in clinical development. Despite its progress, a valuable therapeutic niche remains outside its scope: the mammalian cell. While in vitro systems, phage, bacteria, and yeast have lent themselves to laboratory manipulation, mammalian cells have proven less tractable. Consequently, the power of evolution remains inaccessible to drug development pipelines that seek to modulate mammalian cell signaling. Further, many directed evolution campaigns result in biomolecules that fail in critical ways when transplanted to human cells. To address these limitations and advance methods in drug discovery, I will explore and mine viral diversity to create a novel system for molecular evolution in mammalian cells. Next, focusing on the 5-HT2A serotonin receptor, I will create extracellular nanobodies to template a drug discovery campaign via structural determination and in silico docking. The insights gained by these studies will be applied toward the directed evolution of state-specific nanobodies against dark GPCRs. This work will result in a general method for directed evolution in mammalian cells, chemical matter against HTR2A, and new paths forward for the deorphanization of GPCRs.

Key facts

NIH application ID
10909940
Project number
5K99GM149931-02
Recipient
UNIV OF NORTH CAROLINA CHAPEL HILL
Principal Investigator
Daniel Dewran Kocak
Activity code
K99
Funding institute
NIH
Fiscal year
2024
Award amount
$98,161
Award type
5
Project period
2023-09-01 → 2025-08-31