Dendritic cell therapy for GvHD

NIH RePORTER · NIH · R41 · $299,989 · view on reporter.nih.gov ↗

Abstract

Abstract. Hematologic malignancies are often treated with allogeneic hematopoietic stem cell transplantation (HSCT). However, HSCT is complicated by graft-vs-host disease (GvHD), a severe, potentially lethal complication initiated when donor alloreactive T cells attack host cells and organs. Despite the administration of prophylactic regimens for aGVHD as standard pre- transplantation therapy, up to 60% of these patients develop aGVHD of grade II or higher, and require additional immunosuppressive intervention. Thus, there is an urgent need to improve pre-transplantation therapies to prevent aGVHD. We identified a probiotic exopolysaccharide (EPS) that induces tolerogenic dendritic cells (DCs) that inhibit T cell proliferation, and we found that EPS-treated human DCs (EPS-DCs) both inhibited T cell proliferation in mixed lymphocyte reactions, and significantly increased survival of humanized NSG-HLA-A2 mice after transplantation with human peripheral blood mononuclear cells (hPBMC). The data indicate that a cell-based therapy using EPS-DCs can mitigate aGvHD, and the goal of this Phase I R41 grant is to determine the in vivo fate of EPS-DCs and optimize protection from GvHD by these EPS-DCs; optimize treatment to maximize the graft vs leukemia response; and establish DC and T cell biomarkers of EPS-mediated suppression of GvHD. These studies will provide a novel cell-based therapy for preventing GvHD in patients receiving HSCT. This cell therapy will be translatable to humans because large numbers of EPS-DCs can be generated and frozen in bulk and used as “off the shelf” treatment, for all patients, independent of MHC types.

Key facts

NIH application ID
10918512
Project number
1R41AI179340-01A1
Recipient
HASENTECH, INC.
Principal Investigator
Katherine L. Knight
Activity code
R41
Funding institute
NIH
Fiscal year
2024
Award amount
$299,989
Award type
1
Project period
2024-05-07 → 2026-04-30