Targeted Suppression of Microtubule Dynamics for Treatment of Metastatic Castration-Resistant Prostate Cancer

NIH RePORTER · CA · R01 · $567,145 · view on reporter.nih.gov ↗

Abstract

PROJECT SUMMARY The goal of this proposal is to develop a targeted therapy for treatment of metastatic castration-resistant prostate cancer (mCRPC). There is currently no cure for this disease and available therapies leave significant room for improvement based on dismal survival rates. Prostate-specific membrane antigen (PSMA) is a clinically validated molecular target for diagnostic and therapeutic purposes based on its significant overexpression in PCa tissue compared to normal cells. Glutamate-ureido-based small molecules have exceptional affinity for PSMA and have been labeled with radionuclides to enable targeted tumor detection and therapy. The small molecule 177Lu- PSMA-617 (cytotoxic beta radiation emitter) recently gained FDA-approval for PSMA-targeted radioligand therapy (RLT) of mCRPC. However, despite its initial antitumor activity, disease progression following 177Lu- PSMA-617 RLT occurs in virtually all patients and led to the development of the more potent RLT agent 225Ac- PSMA-617, where the alpha-emitting radionuclide 225Ac provides stronger DNA damaging capabilities. Although recent clinical data with 225Ac-PSMA-617 showed favorable responses, disease progression was still observed. Furthermore, non-tumor binding of 225Ac-PSMA-617 causes considerable damage to the salivary glands and leads to life-long xerostomia in a large percentage of patients. Since PSMA expression often remains actionable as a tumor target following RLT, the development of a non-radioactive targeted therapy could extend the therapeutic benefits of PSMA targeting without the associated risk of organ irradiation. Given the absence of a validated PSMA-targeted drug conjugate, we used PSMA-617 as the foundation for a drug conjugate containing the microtubule inhibitor monomethyl auristatin E (MMAE) and a custom macrocyclic linker known as MMC (multimodality chelator) to enable direct radiolabeling for imaging and quantitative analyses. We provide strong preliminary evidence of PS

Key facts

NIH application ID
11321671
Project number
5R01CA298343-02
Recipient
UNIVERSITY OF TEXAS HLTH SCI CTR HOUSTON
Principal Investigator
Ali Azhdarinia
Activity code
R01
Funding institute
CA
Fiscal year
2026
Award amount
$567,145
Award type
5
Project period
2025-04-15T00:00:00 → 2030-03-31T00:00:00