Rational Translation of EZH2 Targeted Therapy in Germinal Center B-cell Lymphoma

NIH RePORTER · NIH · K08 · $171,180 · view on reporter.nih.gov ↗

Abstract

This proposal describes a 5-year training program designed to enable the applicant to develop an independent research career in the field of lymphoma biology and experimental therapeutics. The applicant is a pediatric oncologist at Weill Cornell Medical College (WCMC) who is committed to an academic career studying disease mechanisms in lymphoma and exploiting these mechanisms to develop novel therapies. Her current research focuses on targeting the histone methyltransferase EZH2 in B-cell lymphoma. The candidate’s immediate career goals are to gain further training in experimental design and develop expertise in epigenomics. Her long-term career goals are to establish independent laboratory space, lead a team of researchers, and make scientific contributions that allow her develop into a national/international leader in the field. To enable these goals this proposal outlines the following career development objectives: 1) formal training in experimental design, drug development, and statistical genomics; 2) coursework in epigenetic dysregulation, 3) regular meetings with an advisory committee composed of distinguished clinicians, scientists, and institutional leaders; 4) formal and informal professional development in leadership, management skills, public speaking and grantsmanship. The applicant’s mentors, Dr. Ethel Cesarman and Dr. Ari Melnick, are both tenured professors at WCMC and are international leaders in the study of viral-related lymphomas and epigenetic mechanisms in lymphoma respectively. Dr. Cesarman and Dr. Melnick have an extensive track record of collaboration including multiple joint grant awards and joint mentorship of trainees. The research proposal focuses on the rational translation of EZH2 targeted therapy in germinal center (GC) B-cell lymphomas. GC B-cell lymphomas are aggressive tumors that occur in pediatrics and adults. Relapsed/refractory disease represents an unmet need with most treatments failing to induce durable remissions. GC B-cell lymphomas are dependent on EZH2 which is a lineage factor for germinal center B-cells. EZH2 may play a unique role in EBV+ lymphoma where it contributes to restricted EBV viral latency that allows immune evasion. Small molecule inhibitors of EZH2 are currently in clinical development, including GSK126, which is being studied in a phase I trial that the applicant is conducting in collaboration with GSK. The unique mechanism and time course of epigenetic therapy requires careful consideration for effective clinical deployment. The overarching goal of this proposal is to develop a rational approach for the clinical use of EZH2i in lymphoma. The specific aims are 1) Define the epigenetic and transcriptional background of lymphomas that respond to EZH2 inhibition (EZH2i); 2) Determine the kinetics of response to EZH2i and the point of maximum vulnerability to combination therapy; 3) Determine the impact of EZH2i on the vulnerability of EBV + lymphomas to immune mediated therapy. Overall ...

Key facts

NIH application ID
9989804
Project number
5K08CA219473-04
Recipient
WEILL MEDICAL COLL OF CORNELL UNIV
Principal Investigator
Lisa Giulino Roth
Activity code
K08
Funding institute
NIH
Fiscal year
2020
Award amount
$171,180
Award type
5
Project period
2017-07-06 → 2021-08-31