Gene Therapy for the Treatment of Fanconi's Anemia Type C

NCT00001399 · clinicaltrials.gov ↗

PHASE1

Phase

COMPLETED

Status

9

Enrollment

NIH

Sponsor class

Conditions

Fanconi's Anemia
Pancytopenia

Interventions

DRUG: Transduced CD34+ Cells

Sponsor

National Heart, Lung, and Blood Institute (NHLBI)