Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency

Conditions

• Ornithine Transcarbamylase Deficiency Disease

Interventions

• GENETIC: recombinant adenovirus containing the ornithine transcarbamylase gene

Sponsor

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

Collaborators

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