Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

NCT00007020 · clinicaltrials.gov ↗

PHASE3

Phase

COMPLETED

Status

85

Enrollment

INDUSTRY

Sponsor class

Conditions

Infantile Refsum's Disease
Zellweger Syndrome
Adrenoleukodystrophy
Peroxisomal Disorders
Cholestasis

Interventions

DRUG: Cholic Acids

Sponsor

Mirum Pharmaceuticals, Inc.

Collaborators

[object Object]