Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

NCT00494195 · clinicaltrials.gov ↗

PHASE1

Phase

COMPLETED

Status

6

Enrollment

OTHER

Sponsor class

Conditions

Muscular Dystrophies

Interventions

GENETIC: rAAV1.tMCK.human-alpha-sarcoglycan- First cohort
GENETIC: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort

Sponsor

Nationwide Children's Hospital

Collaborators

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