Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I

NCT00786968 · clinicaltrials.gov ↗

PHASE1

Phase

TERMINATED

Status

3

Enrollment

INDIV

Sponsor class

Stopped Due to slow enrolment.

Conditions

Spinal Cord Compression
Mucopolysaccharidosis I
Hurler-Scheie Syndrome
Scheie Syndrome
Lysosomal Storage Disease

Interventions

DRUG: laronidase

Sponsor

Patricia I. Dickson, M.D.

Collaborators

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