A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I

NCT00852358 · clinicaltrials.gov ↗

NA

Phase

COMPLETED

Status

9

Enrollment

INDIV

Sponsor class

Conditions

Cognitive Decline
Mucopolysaccharidosis I
Hurler-Scheie Syndrome
Scheie Syndrome
Lysosomal Storage Disease

Interventions

DRUG: laronidase

Sponsor

Patricia I. Dickson, M.D.

Collaborators

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