Gene Therapy ADA Deficiency

NCT01279720 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

COMPLETED

Status

8

Enrollment

OTHER

Sponsor class

Conditions

Adenosine Deaminase Deficiency

Interventions

BIOLOGICAL: Intravenous infusion of transduced cells

Sponsor

Great Ormond Street Hospital for Children NHS Foundation Trust