Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa

NCT01288027 · clinicaltrials.gov ↗

PHASE4

Phase

COMPLETED

Status

16

Enrollment

INDUSTRY

Sponsor class

Conditions

Pompe Disease (Late-Onset)
Glycogen Storage Disease Type II (GSD II)
Glycogenesis 2 Acid Maltase Deficiency

Interventions

BIOLOGICAL: Alglucosidase Alfa

Sponsor

Genzyme, a Sanofi Company