A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype
NCT01358370
·
clinicaltrials.gov ↗
COMPLETED
Status
40
Enrollment
INDUSTRY
Sponsor class
Conditions
Lysosomal Acid Lipase Deficiency
Wolman Disease
Sponsor
Alexion Pharmaceuticals, Inc.