Gene Therapy for X-linked Severe Combined Immunodeficiency
NCT01410019
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
5
Enrollment
OTHER
Sponsor class
Conditions
X-linked Severe Combined Immunodeficiency
Interventions
OTHER:
Gene transfer
Sponsor
Assistance Publique - Hôpitaux de Paris