Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants

NCT01512888 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

SUSPENDED

Status

28

Enrollment

OTHER

Sponsor class

Stopped voluntary hold

Conditions

Severe Combined Immunodeficiency Disease, X-linked

Interventions

GENETIC: CL20-i4-EF1α-hγc-OPT
DRUG: Busulfan
DEVICE: CliniMacs

Sponsor

St. Jude Children's Research Hospital

Collaborators

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