Phenylbutyrate Therapy for Maple Syrup Urine Disease

NCT01529060 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

COMPLETED

Status

20

Enrollment

OTHER

Sponsor class

Conditions

Maple Syrup Urine Disease

Interventions

DRUG: Phenylbutyrate
DRUG: Placebo powder

Sponsor

Brendan Lee