Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia
Stopped insufficient enrollment
Conditions
- Propionic Acidemia
- Methylmalonic Acidemia
Interventions
- DRUG: N-carbamylglutamate
- OTHER: Standard of Care
Sponsor
Mendel Tuchman
Collaborators
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