Lysosomal Acid Lipase (LAL) Deficiency Registry
Conditions
- Lysosomal Acid Lipase Deficiency
- Cholesterol Ester Storage Disease
- Wolman Disease
- Acid Cholesteryl Ester Hydrolase Deficiency, Type 2
- Acid Lipase Deficiency
- LIPA Deficiency
- LAL-Deficiency
Sponsor
Alexion Pharmaceuticals, Inc.