Natural History Study of Children With Metachromatic Leukodystrophy
Stopped Enrollment issues
Conditions
- Lipid Metabolism Disorders
- Metachromatic Leukodystrophy (MLD)
- Nervous System Diseases
- Brain Diseases
- Central Nervous System Diseases
- Demyelinating Diseases
- Metabolism, Inborn Errors
- Genetic Diseases, Inborn
- Sphingolipidoses
- Hereditary Central Nervous System Demyelinating Diseases
- Metabolic Inborn Brain Diseases
- Lysosomal Storage Diseases
- Metabolic Diseases
- Sulfatidosis
Sponsor
Shire