A Pilot Study of Pyridostigmine in Pompe Disease
NCT02357225
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
TERMINATED
Status
2
Enrollment
OTHER
Sponsor class
Stopped
The drug was ineffective in improving function in Pompe's disease
Conditions
Pompe Disease
Interventions
DRUG:
Pyridostigmine Bromide
Sponsor
University of Florida