Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy

NCT02376816 · clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
2
Enrollment
OTHER
Sponsor class

Conditions

Interventions

Sponsor

Jerry R. Mendell

Collaborators