Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2
NCT02704325
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
WITHDRAWN
Status
OTHER
Sponsor class
Conditions
Duchenne Muscular Dystrophy
Interventions
BIOLOGICAL:
rAAVrh74.MCK.GALGT2
OTHER:
PLACEBO (Saline)
Sponsor
Kevin Flanigan